Pipeline

SpliSense solutions treat the root cause of the disease – the mutation or proteins– to eliminate disease symptoms and improve patients’ Quality of Life (QOL). Our platform can restore protein functionality by increasing the level of mature functional proteins or reducing expression of target proteins. This is performed by modulating the splicing pattern of genes which cause or affect pulmonary diseases.
Our most advanced programs focus on high unmet need, orphan indications in Cystic Fibrosis (CF), with subsequent expansion to larger, non-orphan pulmonary indications (muco- obstructive diseases).

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